The U.S. Food and Drug Administration approved Kebilidi (eladocagene exuparvovec-tneq), an adeno-associated virus ...

The Veterans Mental Health Steering Committee is requesting information from current veterans’ mental health, substance use, ...

Data from the National Health Authority shows that nearly 6.5 lakh elderly individuals have successfully enrolled and ...

Georgetown faces the Notre Dame Fighting Irish after Thomas Sorber scored 25 points in Georgetown's 69-57 win against the Fairfield Stags. The teams meet Saturday for the first time this ...

PTC Therapeutics’ gene therapy, Kebilidi to treat AADC deficiency receives US FDA approval: Warren, New Jersey Friday, November 15, 2024, 10:00 Hrs [IST] PTC Therapeutics, Inc., ...

Becca Ziegler is only 24, but she already has her death planned out: her corpse will be deep-frozen to minus 200 degrees ...

The Food and Drug Administration (FDA) has granted accelerated approval to Kebilidi™ (eladocagene exuparvovec-tneq) for the treatment of adult and pediatric patients with aromatic L-amino acid ...

At the BioFuture 2024 conference held in New York in November, Seema Kumar, the CEO of Cure, described women’s health as something that has been directed at the “bikini area.” That “bikini” bias ...

PTC Therapeutics' Kebilidi gains FDA accelerated approval as the first brain-administered gene therapy in the U.S. for AADC ...

This is the first gene therapy for AADC deficiency to receive US regulatory approval and the first that can be administered directly to the brain.

The drug is a treatment for a rare and fatal genetic disorder called aromatic l-amino acid decarboxylase (AADC) deficiency, ...